Human C9ORF72 hexanucleotide expansion reproduces RNA foci and dipeptide repeat proteins but not neurodegeneration in BAC transgenic mice OM Peters, GT Cabrera, H Tran, TF Gendron, JE McKeon, J Metterville, ... Neuron 88 (5), 902-909, 2015 | 282 | 2015 |
Editing out five Serpina1 paralogs to create a mouse model of genetic emphysema F Borel, H Sun, M Zieger, A Cox, B Cardozo, W Li, G Oliveira, A Davis, ... Proceedings of the National Academy of Sciences 115 (11), 2788-2793, 2018 | 80 | 2018 |
Safe and effective superoxide dismutase 1 silencing using artificial microRNA in macaques F Borel, G Gernoux, H Sun, R Stock, M Blackwood, RH Brown Jr, ... Science Translational Medicine 10 (465), eaau6414, 2018 | 74 | 2018 |
Defining the transcriptional and post-transcriptional landscapes of Mycobacterium smegmatis in aerobic growth and hypoxia MC Martini, Y Zhou, H Sun, SS Shell Frontiers in microbiology 10, 426725, 2019 | 65 | 2019 |
Safe and efficient silencing with a Pol II, but not a Pol lII, promoter expressing an artificial miRNA targeting human huntingtin EL Pfister, KO Chase, H Sun, LA Kennington, F Conroy, E Johnson, ... Molecular Therapy-Nucleic Acids 7, 324-334, 2017 | 33 | 2017 |
Enhanced residual networks for context-based image outpainting P Gardias, E Arthur, H Sun arXiv preprint arXiv:2005.06723, 2020 | 5 | 2020 |
The small non-coding RNA B11 regulates multiple facets of Mycobacterium abscessus virulence M Bar-Oz, MC Martini, MN Alonso, M Meir, NI Lore, P Miotto, C Riva, ... Plos Pathogens 19 (8), e1011575, 2023 | 3 | 2023 |
RNA sequencing for transcript 5′-end mapping in mycobacteria MC Martini, H Sun, SS Shell Mycobacteria Protocols, 513-531, 2021 | 3 | 2021 |
Mycobacterial RNase E cleaves with a distinct sequence preference and controls the degradation rates of most Mycolicibacterium smegmatis mRNAs Y Zhou, H Sun, AR Rapiejko, DA Vargas-Blanco, MC Martini, MR Chase, ... Journal of Biological Chemistry 299 (11), 2023 | | 2023 |
Defining the transcriptional and post-transcriptional landscapes of Mycobacterium smegmatis in aerobic growth and oxygen limitation MC Martini, Y Zhou, H Sun, SS Shell bioRxiv, 423392, 2018 | | 2018 |
Editing out Five SERPINA1 Paralogs to Create a New Mouse Model of Genetic Emphysema F Borel, H Sun, MK Elmallah, A Cox, B Cardozo, W Li, AM Hoffman, ... MOLECULAR THERAPY 25 (5), 117-117, 2017 | | 2017 |
183. Developing Strategies To Improve the Current Clinical Vector AAV1-CB-AAT for Alpha-One Antitrypsin Deficiency F Borel, S Choudhury, G Aslanidi, L Song, E Kocabas, H Sun, Q Tang, ... Molecular Therapy 23, S73, 2015 | | 2015 |