Nusinersen in the treatment of spinal muscular atrophy K Goodkey, T Aslesh, R Maruyama, T Yokota Exon skipping and inclusion therapies: Methods and protocols, 69-76, 2018 | 50 | 2018 |
Skipping multiple exons to treat DMD—promises and challenges T Aslesh, R Maruyama, T Yokota Biomedicines 6 (1), 1, 2018 | 45 | 2018 |
Restoring SMN expression: an overview of the therapeutic developments for the treatment of spinal muscular atrophy T Aslesh, T Yokota Cells 11 (3), 417, 2022 | 40 | 2022 |
Development of DG9 peptide-conjugated single-and multi-exon skipping therapies for the treatment of Duchenne muscular dystrophy KRQ Lim, S Woo, D Melo, Y Huang, K Dzierlega, MNA Shah, T Aslesh, ... Proceedings of the National Academy of Sciences 119 (9), e2112546119, 2022 | 25 | 2022 |
eSkip-Finder: a machine learning-based web application and database to identify the optimal sequences of antisense oligonucleotides for exon skipping S Chiba, KRQ Lim, N Sheri, S Anwar, E Erkut, MNA Shah, T Aslesh, ... Nucleic Acids Research 49 (W1), W193-W198, 2021 | 18 | 2021 |
Restoration of dystrophin expression and correction of Duchenne muscular dystrophy by genome editing T Aslesh, E Erkut, T Yokota Expert Opinion on Biological Therapy 21 (8), 1049-1061, 2021 | 15 | 2021 |
Development of antisense oligonucleotide gapmers for the treatment of Huntington’s disease T Aslesh, T Yokota Gapmers: Methods and Protocols, 57-67, 2020 | 10 | 2020 |
Development of antisense oligonucleotide gapmers for the treatment of dyslipidemia and lipodystrophy T Aslesh, T Yokota Gapmers: Methods and Protocols, 69-85, 2020 | 10 | 2020 |
DG9-conjugated morpholino rescues phenotype in SMA mice by reaching the CNS via a subcutaneous administration T Aslesh, E Erkut, J Ren, KRQ Lim, S Woo, S Hatlevig, HM Moulton, ... JCI insight 8 (5), 2023 | 5 | 2023 |
Systemic and ICV injections of antisense oligos into SMA mice and evaluation T Aslesh, R Maruyama, T Yokota Exon Skipping and Inclusion Therapies: Methods and Protocols, 455-465, 2018 | 2 | 2018 |
An indian perspective of some recent developments in polio, dpt, zika and rotavirus vaccines VV Iyer, A Tejal, A Poddar, D Maithili, LG Rasika, A Bendre, V Jaswal Indian J Pharm Sci 79 (2), 175-185, 2017 | 1 | 2017 |
Assessing the Role of Aquaporin 4 in Skeletal Muscle Function T Aslesh, A Al-Aghbari, T Yokota International Journal of Molecular Sciences 24 (2), 1489, 2023 | | 2023 |